NEW YORK – CA19-9 blood tests are a common way to screen for pancreatic cancer and monitor treatment, but researchers in Taiwan say common thresholds may ignore patients who have naturally lower ...

Every day, your liver assembles billions of tiny cholesterol-carrying particles and ships them into your blood. How many it ...

FDA-approved EB therapies expand options for gene replacement and wound healing, but success depends on careful wound preparation and timing, experts say.

Scientists used CRISPR technology to disable the cholesterol gene in a groundbreaking study, though widespread availability ...

Neurological diseases represent a broad and growing class of disorders, whose prevalence is expected to rise in the coming years due to population aging and ...

A major international study has uncovered several new genetic clues tied to hyperemesis gravidarum, a debilitating form of ...

A planned first-in-human trial aims to treat GM1 gangliosidosis in utero, possibly laying the foundation for prenatal gene ...

The recent approval of Regeneron’s Otarmeni underscores the maturation of gene therapies across a range of diseases. Here, ...

The principal investigator reported at the ASGCT meeting that the study met its primary endpoint, though there were two treatment-related serious adverse events.

Combining pre-formed vesicles with nucleic acid cargo at the point of care can remove long-standing barriers to personalized ...

Genetically engineered cultured host cells containing recombinant nucleic acids useful for gene therapy are patent-eligible for being ...

Reaffirmed FDA alignment on TSHA-102 BLA pathway, including pivotal trial design, endpoints and potential to submit for approval based on REVEAL ...