Nine-month-old KJ Muldoon is the first patient to successfully receive personalized CRISPR gene editing therapy. After 300 ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...

KJ Muldoon's life-threatening disorder, called severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, was treated with ...

After 307 days at the Children's Hospital of Philadelphia, a local baby who was born with a rare and usually fatal disorder ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that won the Nobel Prize five years ago.

Baby KJ Muldoon was born with a rare genetic disorder called CPS1 deficiency and spent nearly the entire first year of his life in the hospital. Now, he’s finally home after becoming the first patient ...

Within minutes of KJ Muldoon’s birth, doctors knew there was something very wrong. Five weeks premature, his little arms went rigid when lifted and shook oddly on the way back down. An attentive ...

The baby, KJ Muldoon of Clifton Heights, Pennsylvania, is one of 350 million people worldwide with rare diseases, most of which are genetic. Now he’s the first patient to be treated with CRISPR ...