The FDA approved labeling changes for elivaldogene autotemcel (eli-cel; Skysona), a one-time gene therapy for patients with early, active cerebral adrenoleukodystrophy (CALD), to reflect new safety ...

Once dismissed as “junk” DNA, ancient viruses embedded in the human genome play a key role in early human development, ...

Q2 2025 Earnings Call Transcript August 7, 2025 Insmed Incorporated misses on earnings expectations. Reported EPS is $-1.7 ...

Net loss (GAAP) widened to $2.6 million, driven by increased expenses from the GPCR Therapeutics USA Inc. acquisition. Management issued a going concern warning, citing $7.9 million in cash and cash ...

Neuroblastoma can be a particularly insidious cancer. In about half of all cases, tumors regress, even without therapy. In ...

The most comprehensive genetic study to date on stuttering has established a clear genetic connection to the condition, ...

Presented preclinical data at the American Society of Clinical Oncology (ASCO) on CLD-401 demonstrating biological efficacy IL-15 superagonist delivery to metastatic tumor sites and reduced immune cle ...

A study led by Roswell Park Comprehensive Cancer Center helps explain why a rare and hyper-aggressive subtype of kidney cancer is susceptible to immunotherapy—information that helped researchers ...