European Medical Journal

CRISPR Gene Therapy Shows Promise in Sickle Cell Disease

CRISPR gene therapy increases haemoglobin and fetal haemoglobin in sickle cell disease, reducing vaso occlusive events in ...

Countable Labs Addresses Critical Measurement Gaps in Cell and Gene Therapy

Countable Labs announces ASGCT plans, proof of concept assay services, and grant program, helping address measurement gaps in cell and gene therapy.
Scientific American

How scientists made the discoveries behind a game-changing gene therapy for sickle cell disease

Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle ...
STAT

Scientists link boy’s tumor to gene therapy viruses, in rare finding

Doctors have linked a boy's tumor to a gene therapy, but say the rare risks need to be weighed against the profound benefits ...

Health breakthroughs: FDA approves gene therapy that restores child hearing

Dr. Marty Makary noted it had "record speed approval," the fastest approval of any gene therapy device combination in U.S.
Clinical Trials Arena on MSN

Fractyl Health’s GLP-1 gene therapy trial given green light

Fractyl believes its AAV GLP-1 gene therapy is the first of its kind to enter clinical trials.

Gene therapy for a rare type of deafness shows lasting results

Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have persisted for more than two years for some patients.
Medscape

Gene-Agnostic Therapy Sees 3-year Gain in Severe Vision Loss

A treatment that targets dysfunctional photoreceptors regardless of the underlying genetic mutation leads to improved ...

New Gene Therapy Can Restore Hearing in Deaf Kids—And It Comes With an Unexpected Price Tag

A breakthrough FDA-approved treatment is changing how genetic deafness is treated.

Bayer Advances Gene Therapy Imaging And Crop Alliance In Long Term Story

Bayer (XTRA:BAYN) subsidiary AskBio has begun dosing patients in a clinical trial of an investigational gene therapy for late ...

First-ever gene therapy for hearing loss gets FDA approval: 'Groundbreaking'

The FDA has approved Otarmeni, the first-ever gene therapy for genetic hearing loss caused by the OTOF gene, for both pediatric and adult patients after positive results.