Nine-month-old KJ Muldoon is the first patient to successfully receive personalized CRISPR gene editing therapy. After 300 ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...

KJ Muldoon's life-threatening disorder, called severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, was treated with ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

Baby KJ was successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

So-called “less-lethal” weapons like those that have been used against demonstrators in Los Angeles can cause severe, lasting ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

Gene therapy experts and advocates warning of the sector’s many challenges found a receptive audience in FDA leadership at a ...

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

Scientists were able to create a bespoke treatment for KJ Muldoon’s rare genetic disorder within six months. It could be a ...